In vitro evaluation of novel antisense oligonucleotides is predictive of in vivo exon skipping activity for Duchenne muscular dystrophy.
Wang, Qingsong 1,2,+; Yin, HaiFang *,2,3,+; Camelliti, Patrizia 2; Betts, Corinne 2; Moulton, Hong 4; Lee, Hyunil 5; Saleh, Amer F. 6; Gait, Michael J. 6; Wood, Matthew J. A. *,2
[Article]
The Journal of Gene Medicine.
12(4):354-364, April 2010.
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