Targeted gene correction of [alpha]1-antitrypsin deficiency in induced pluripotent stem cells.
Yusa, Kosuke K; Rashid, Tamir S T S.; Strick-Marchand, Helene H; Varela, Ignacio I; Liu, Pei-Qi P; Paschon, David D E E.; Miranda, Elena E; Ordonez, Adriana A; Hannan, Nicholas N R F R. F.; Rouhani, Foad F J J.; Darche, Sylvie S; Alexander, Graeme G; Marciniak, Stefan S J J.; Fusaki, Noemi N; Hasegawa, Mamoru M; Holmes, Michael M C C.; Di Santo, James J P P.; Lomas, David D A A.; Bradley, Allan A; Vallier, Ludovic L
[Letter]
Nature.
478(7369):391-394, October 20, 2011.
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